Approval For Duchenne Muscular Dystrophy Treatment, Translarna

EDM number 1382 in 2015-16, proposed by Mary Glindon on 18/04/2016.
Categorised under the topics of Diseases and Health services.

That this House welcomes the decision by the National Institute for Health and Care Excellence (NICE) to recommend the Duchenne muscular dystrophy treatment, Translarna, for funding by NHS England, as a result of a Managed Access Agreement; notes that Translama is the first ever approved drug to treat an underlying genetic cause of Duchenne muscular dystrophy; recognises the tireless campaigning by patients and families throughout the NHS England and NICE processes calling for access to Translama; acknowledges the vital role that Muscular Dystrophy UK and Action Duchenne have played as patient organisation stakeholders during the NICE assessment process; further recognises the role of other charities in pressing for access to Translama; further notes with concern the announcement by the Scottish Medicines Consortium to recommend that Translarna not be approved for funding by NHS Scotland; and calls on NHS England to shorten implementation from three months so that the drug is available as quickly as possible.

This motion has been signed by a total of 28 MPs.